Scientific publications
Givosiran - Running RNA Interference to Fight Porphyria Attacks
Jun 11, 2020
| Magazine: The New England Journal of Medicine
Gloria Gonzalez-Aseguinolaza
No abstract available.
CITATION Gut. 2019 Nov;68(11):1913-1914. doi: 10.1136/gutjnl-2019-319410. Epub 2019 Aug 2.

Our authors
Senior Researcher | Principal Investigator
Gene Therapy and Regulation of Gene Expression Research Program