Research Projects
Optimization of messenger RNA trans-splicing for the treatment of genetic encephalopathies
Researcher | Principal Investigator
Gene Therapy for Monogenic Encephalopathies Research Group
Research Division
DNA and RNA Medicine Division
Research program
Gene Therapy for Rare Diseases
Project information
“Optimization of messenger RNA trans-splicing for the treatment of genetic encephalopathies” is a project of the Gene Therapy for Congenital Encephalopathies research group, which is part of the Gene Therapy for Rare Diseases research program.
Project PID2024-160352OB-I00 funded by:
- Convocation: Proyectos de Generación de Conocimiento 2024
- Reference: PID2024-160352OB-I00
- Start date: September 1, 2025
- End date: August 31, 2028
- Nature of project: National

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